Présentations Powerpoint

10 ANS DE DEPISTAGE NEONATAL A BRUXELLES
30 avril f
6 HLA et DPI
la drépanocytose De l'enfant à l'adulte
Suivi prospectif cohorte
Utilisation de chambres implantables chez 14 enfants drépanocytaires

Articles

Day SW. Development and evaluation of a sickle cell assessment instrument.Pediatr Nurs. 2004 Nov-Dec;30(6):451-8.
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15704592

Fitzhugh CD, Wigfall DR, Ware RE. Enalapril and hydroxyurea therapy for children with sickle nephropathy.Pediatr Blood
Cancer. 2005 Feb 9;
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15704213

Bernaudin F, Verlhac S, Coic L, Lesprit E, Brugieres P, Reinert P. Long-term follow-up of pediatric sickle cell disease patients
with abnormal high velocities on transcranial Doppler. Pediatr Radiol. 2005 Feb 10
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15703901

Raj A, Bertolone S, Bond S, Burnett D, Denker A. Cathlink(R) 20: A subcutaneous implanted central venous access device
used in children with sickle cell disease on long-term erythrocytapheresis-a report of low complication rates.Pediatr Blood
Cancer. 2005 Feb 7;
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15700248

Pawloski JR, Hess DT, Stamler JS. Impaired vasodilation by red blood cells in sickle cell disease.Proc Natl Acad Sci U S A.
2005 Feb 7 http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15699345

Adorno EV, Couto FD, Moura Neto JP, Menezes JF, Rego M, Reis MG, Goncalves
MS. Hemoglobinopathies in newborns from Salvador, Bahia, Northeast Brazil.Cad Saude Publica. 2005 Feb;21(1):292-298.
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15692663

Osby M, Shulman IA.Phenotype matching of donor red blood cell units for nonalloimmunized sickle cell disease patients: a
survey of 1182 North American laboratories.Arch Pathol Lab Med. 2005 Feb;129(2):190-3.
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15679419

Marie J Stuart, Ronald L Nagel. Sickle-cell disease - www.thelancet.com Vol 364 October 9, 2004 - Lancet Seminar article
on Sickle Cell Disease. http://www.scinfo.org/LancetSeminar.pdf

R.E. Eckart, S.L. Scoville, C.L. Campbell, E.A. Shry, K.C. Stajduhar, R.N. Potter, L.A. Pearse, and R. Virman Sudden Death in Young Adults: A 25-Year Review of Autopsies in Military Recruits 7 December 2004 issue of Annals of Internal Medicine (volume 141, pages 829-834) - n 44 of the 126 recruits who died, examination of medical records and autopsy results revealed no explanation for the death. Other causes of death included sickle-cell crisis (3 deaths) http://www.annals.org/cgi/content/summary/141/11/829

Wagner MC, Eckman JR, Wick TM. Sickle cell adhesion depends on hemodynamics and endothelial activation. J Lab Clin Med. 2004 Nov;144(5):260-7.
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15570244

Buchanan GR, Debaun MR, Quinn CT, Steinberg MH. Sickle cell disease.Hematology (Am Soc Hematol Educ Program). 2004;:35-47. An excellent review available Full Text by PDF or HTML at http://www.asheducationbook.org/cgi/reprint/2004/1/35
Kaur N, Motwani B, Sivasubramaniam D, Feldman L, Allen S, Ferguson R, Shiomoto
G, Ansell D, Westerman M, Feldman L. Potential role of the ventilation and perfusion (V/Q) lung scan in the diagnosis of acute chest syndrome in adults with sickle cell disease. Am J Hematol. 2004 Dec;77(4):407-9.
http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15551281

Christoph GW, Hofrichter J, Eaton WA. Understanding the shape of sickled red cells. Biophys J. 2004 Nov 12; Full Text at
http://www.biophysj.org/cgi/rapidpdf/biophysj.104.051250v1

Nelson J. Chao, Stephen G. Emerson, and Kenneth I. Weinberg Stem Cell Transplantation (Cord Blood Transplants) Hematology 2004:354-371 Full Text at http://www.asheducationbook.org/cgi/content/abstract/2004/1/354

Gladwin MT, Sachdev V, Jison ML, Shizukuda Y, Plehn JF, Minter K, Brown B, Coles WA, Nichols JS, Ernst I, Hunter LA,
Blackwelder WC, Schechter AN, Rodgers GP, Castro O, Ognibene FP
Pulmonary hypertension as a risk factor for death in patients with sickle cell disease.N Engl J Med. 2004 Feb 26;350(9):886-95.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=14985486

Maples BL, Hagemann TM.
Treatment of priapism in pediatric patients with sickle cell disease. Am J Health Syst Pharm. 2004
Feb 15;61(4):355-63.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15011763

Thurston GB, Henderson NM, Jeng M.
Effects of erythrocytapheresis transfusion on the viscoelasticity of sickle cell blood.
Clin Hemorheol Microcirc. 2004;30(2):83-97.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15004333

Kaul DK, Liu XD, Choong S, Belcher JD, Vercellotti GM, Hebbel RP.
Anti-inflammatory Therapy Ameliorates Leukocyte Adhesion and Microvascular Flow Abnormalities in Transgenic Sickle Mice. Am J Physiol Heart Circ Physiol. 2004 Mar 4
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=15001449

Segal JB, Miller ER 3rd, Brereton NH, Resar LM.
Concentrations of B vitamins and homocysteine in children with sickle cell anemia. South Med J. 2004 Feb;97(2):149-55.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=14982264

Davies E, Riddington C, Lottenberg R, Dower N.
Pneumococcal vaccines for sickle cell disease.Cochrane Database Syst Rev. 2004;1:CD003885.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=14974042

Brachet C, Azzi N, Demulder A, Devalck C, Gourdin A, Gulbis B, Klein A, Le PQ, Loop M, Sariban E, Ferster
A.
Hydroxyurea treatment for sickle cell disease: impact on haematopoietic stem cell transplantation's outcome.Bone Marrow
Transplant. 2004 Feb 9
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=14767501

Quinn CT, Rogers ZR, Buchanan GR.
Survival of Children with Sickle Cell Disease.Blood. 2004 Feb 5
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=14764527

Gibbs WJ, Hagemann TM.
Purified poloxamer 188 for sickle cell vaso-occlusive crisis.Ann Pharmacother. 2004 Feb;38(2):320-4.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=pubmed&dopt=Abstract&list_uids=14742772

Nagar S, Remmel RP, Hebbel RP, Zimmerman CL.
Metabolism of opioids is altered in liver microsomes of sickle cell transgenic mice. Drug Metab Dispos. 2004 Jan; 32(1): 98-104.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14709626&dopt=Abstract

Melzer-Lange MD, Walsh-Kelly CM, Lea G, Hillery CA, Scott JP.
Patient-controlled analgesia for sickle cell pain crisis in a pediatric emergency department. Pediatr Emerg Care. 2004 Jan; 20(1): 2-4.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14716157&dopt=Abstract

Sylvester KP, Patey RA, Milligan P, Dick M, Rafferty GF, Rees D, Thein SL, Greenough A.
Pulmonary function abnormalities in children with sickle cell disease.Thorax. 2004 Jan; 59(1): 67-70.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14694252&dopt=Abstract

Ataga KI, Orringer EP. Hypercoagulability in sickle cell disease: a curious paradox.
Am J Med. 2003 Dec 15; 115(9): 721-8.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14693325&dopt=Abstract

Sickle Cell research Update - An excellent review of therapy options in sickle cell disease from American Society of Hematology ASH - full text at
http://www.asheducationbook.org/cgi/content/full/2003/1/14

Brugnara C.
Sickle cell disease: from membrane pathophysiology to novel therapies for prevention of erythrocyte dehydration.
J Pediatr Hematol Oncol. 2003 Dec;25(12):927-33.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14663274&dopt=Abstract

West DC, Romano PS, Azari R, Rudominer A, Holman M, Sandhu S.
Impact of environmental tobacco smoke on children with sickle cell disease. Arch Pediatr Adolesc Med. 2003 Dec;157(12):1197-201.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14662575&dopt=Abstract

Schultz WH, Ware RE.
Malignancy in patients with sickle cell disease. Am J Hematol. 2003 Dec;74(4):249-53.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14635205&dopt=Abstract

Atweh GF, DeSimone J, Saunthararajah Y, Fathallah H, Weinberg RS, Nagel RL, Fabry ME, Adams RJ.
Hemoglobinopathies. Hematology (Am Soc Hematol Educ Program). 2003;:14-39. An excellent review of therapy options in sickle cell disease full text at
http://www.asheducationbook.org/cgi/content/full/2003/1/14

Claster S, Vichinsky EP.
Managing sickle cell disease.BMJ. 2003 Nov 15;327(7424):1151-5. An excellent review - Full Text at http://bmj.bmjjournals.com/cgi/content/full/327/7424/1151

Saunthararajah Y, Hillery CA, Lavelle D, Molokie R, Dorn L, Bressler L, Gavazova S, Chen YH, Hoffman R, DeSimone J.
Effects of 5-aza-2'-deoxycytidine on fetal hemoglobin levels, red cell adhesion, and hematopoietic differentiation in patients with sickle cell disease. Blood. 2003 Dec 1;102(12):3865-70. Epub 2003 Aug 07.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12907443&dopt=Abstract

Zimmerman SA, Schultz WH, Davis JS, Pickens CV, Mortier NA, Howard TA, Ware RE.
Sustained long-term hematological efficacy of hydroxyurea at maximal tolerated dose in children with sickle cell disease Blood. 2003 Nov 20 [Epub ahead of print].
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14630791&dopt=Abstract

Adamkiewicz TV, Sarnaik S, Buchanan GR, Iyer RV, Miller ST, Pegelow CH, Rogers ZR, Vichinsky E, Elliott J, Facklam RR, O'brien KL, Schwartz B, Van Beneden CA, Cannon MJ, Eckman JR, Keyserling H, Sullivan K, Wong WY, Wang WC.
Invasive pneumococcal infections in children with sickle cell disease in the era of penicillin prophylaxis, antibiotic resistance, and
23-valent pneumococcal polysaccharide vaccination. J Pediatr. 2003 Oct;143(4):438-44.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14571216&dopt=Abstract

Smith WR, Coyne P, Smith VS, Mercier B.
Temperature changes, temperature extremes, and their relationship to emergency department visits and hospitalizations for sickle cell crisis. Pain Manag Nurs. 2003 Sep;4(3):106-11.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14566708&dopt=Abstract

Carmen R. Green MD, Karen O. Anderson PhD, Tamara A. Baker PhD, Lisa C. Campbell PhD, Sheila Decker PhD, Roger B. Fillingim PhD, Donna A.
Kaloukalani MD, MPH, Kathyrn E. Lasch PhD, Cynthia Myers PhD, Raymond C. Tait PhD, Knox H. Todd MD, MPH, April H. Vallerand PhD, RN The Unequal Burden of Pain: Confronting Racial and Ethnic Disparities in Pain. Pain Medicine Vol. 4 Issue 3 Page 277 September 2003 To download the press release click here Manci EA, Culberson DE, Yang YM, Gardner TM, Powell R, Haynes J, Shah AK, Mankad VN; Investigators of the Cooperative Study of Sickle Cell Disease.
Causes of death in sickle cell disease: an autopsy study. Br J Haematol. 2003 Oct;123(2):359-65.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14531921&dopt=Abstract

Pathare A, Kindi SA, Daar S, Dennison D. Cytokines in sickle cell disease. Hematology. 2003 Oct;8(5):329-37.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14530175&dopt=Abstract

Smith-Whitley K, Zhao H, Hodinka RL, Kwiatkowski J, Cecil R, Cecil T, Cnaan A, Ohene-Frempong K.
The epidemiology of human parvovirus B19 in children with sickle cell disease.Blood. 2003 Oct 2
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=14525777&dopt=Abstract

Steen RG, Emudianughe T, Hankins GM, Wynn LW, Wang WC, Xiong X, Helton KJ.
Brain imaging findings in pediatric patients with sickle cell disease Radiology. 2003 Jul;228(1):216-25. Epub 2003 May 29.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12775848&dopt=Abstract

Steen RG, Hankins GM, Xiong X, Wang WC, Beil K, Langston JW, Helton KJ.
Prospective brain imaging evaluation of children with sickle cell trait: initial observations. Radiology. 2003 Jul;228(1):208-15. Epub 2003 May 20.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12759471&dopt=Abstract

Oniyangi O, Omari A.
Malaria chemoprophylaxis in sickle cell disease.Cochrane Database Syst Rev. 2003;3:CD003489.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12917969&dopt=Abstract

Hasan SP, Hashmi S, Alhassen M, Lawson W, Castro O.
Depression in sickle cell disease. J Natl Med Assoc. 2003 Jul;95(7):533-7.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12911250&dopt=Abstract

Saunthararajah Y, Hillery CA, Lavelle D, Molokie R, Dorn L, Bressler L, Gavazova S, Chen YH, Hoffman R, DeSimone J.
Effects of 5-aza-2'-deoxycytidine on fetal hemoglobin levels, red cell adhesion, and hematopoietic differentiation in patients with sickle cell disease.1: Blood. 2003 Aug 7
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12907443&dopt=Abstract

Morris CR, Vichinsky EP, van Warmerdam J, Machado L, Kepka-Lenhart D, Morris SM Jr, Kuypers FA.
Hydroxyurea and arginine therapy: impact on nitric oxide production in sickle cell disease.J Pediatr Hematol Oncol. 2003 Aug;25(8):629-34.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12902916&dopt=Abstract

Hsu LL, Miller ST, Wright E, Kutlar A, McKie V, Wang W, Pegelow CH, Driscoll C, Hurlet A, Woods G, Elsas L, Embury S, Adams RJ;
Stroke Prevention Trial (STOP) and the Cooperative Study of Sickle Cell Disease (CSSCD). Alpha Thalassemia is associated with decreased risk of abnormal transcranial Doppler ultrasonography in children with sickle cell anemia. J Pediatr Hematol Oncol. 2003 Aug;25(8):622-8.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12902915&dopt=Abstract

Kral MC, Brown RT, Nietert PJ, Abboud MR, Jackson SM, Hynd GW.
Transcranial Doppler ultrasonography and neurocognitive functioning in children with sickle cell disease. Pediatrics. 2003 Aug;112(2):324-31.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12897282&dopt=Abstract

Vermylen C.
Hematopoietic stem cell transplantation in sickle cell disease. Blood Rev. 2003 Sep;17(3):163-6.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12818226&dopt=Abstract

Nagel RL, Fabry ME, Steinberg MH.
The paradox of hemoglobin SC disease.Blood Rev. 2003 Sep;17(3):167-78.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12818227&dopt=Abstract

Neumayr L, Lennette E, Kelly D, Earles A, Embury S, Groncy P, Grossi M, Grover R, McMahon L, Swerdlow P, Waldron P, Vichinsky E.
Mycoplasma disease and acute chest syndrome in sickle cell disease. Pediatrics. 2003 Jul;112(1 Pt 1):87-95.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12837872&dopt=Abstract

Fiorentino F, Magli MC, Podini D, Ferraretti AP, Nuccitelli A, Vitale N, Baldi M, Gianaroli L
The minisequencing method: an alternative strategy for preimplantation genetic diagnosis of single gene disorders.1: Mol Hum Reprod. 2003 Jul;9(7):399-410.
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12802047&dopt=Abstract

Steinberg MH, Barton F, Castro O, Pegelow CH, Ballas SK, Kutlar A, Orringer E,
Bellevue R, Olivieri N, Eckman J, Varma M, Ramirez G, Adler B, Smith W, Carlos T,
Ataga K, DeCastro L, Bigelow C, Saunthararajah Y, Telfer M, Vichinsky E, Claster S, Shurin S, Bridges K, Waclawiw M, Bonds D, Terrin M.
Effect of hydroxyurea on mortality and morbidity in adult sickle cell anemia: risks and benefits up to 9 years of treatment. JAMA 2003 Apr 2;289(13):1645-51
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12672732&dopt=Abstract

Hoppe C, Klitz W, Noble J, Vigil L, Vichinsky E, Styles L.
Distinct HLA associations by stroke subtype in children with sickle cell anemia.Blood 2003 Apr 1;101(7):2865-9
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12517810&dopt=Abstract

Houston-Yu P, Rana SR, Beyer B, Castro O.
Frequent and prolonged hospitalizations: a risk factor for early mortality in sickle cell disease patients.Am J Hematol 2003 Mar;72(3):201-3
http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12605392&dopt=Abstract

Toward gene therapy for beta -thalassemia: new models, new approaches
Punam Malik Blood 2003;101 2902
http://www.bloodjournal.org/cgi/content/full/101/8/2902/a?etoc

Novel epinephrine and cyclic AMP-mediated activation of BCAM/Lu-dependent sickle (SS) RBC adhesion
Patrick C. Hines, Qin Zen, Sharran N. Burney, Deborah A. Shea, Kenneth I. Ataga, Eugene P. Orringer, Marilyn J. Telen, and Leslie V. Parise Blood 2003;101 3281-3287 http://www.bloodjournal.org/cgi/content/abstract/101/8/3281?etoc

Aberrant development of Plasmodium falciparum in hemoglobin CC red cells: implications for the malaria protective effect of the homozygous state
Rick M. Fairhurst, Hisashi Fujioka, Karen Hayton, Kathleen F. Collins, and Thomas E. Wellems Blood 2003;101 3309-3315
http://www.bloodjournal.org/cgi/content/abstract/101/8/3309?etoc

King SB.
The nitric oxide producing reactions of hydroxyurea.Curr Med Chem 2003 Mar;10(6):437-52 http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12570692&dopt=Abstract

Dean D, Neumayr L, Kelly DM, Ballas SK, Kleman K, Robertson S, Iyer RV, Ware RE, Koshy M, Rackoff WR, Pegelow CH, Waldron P, Benjamin L, Vichinsky E;
Acute Chest Syndrome Study Group. Chlamydia pneumoniae and Acute Chest Syndrome in Patients With Sickle Cell Disease. J Pediatr Hematol Oncol 2003 Jan;25(1):46-55 http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12544773&dopt=Abstract

Gaziev J, Lucarelli G.
Stem cell transplantation for hemoglobinopathies.Curr Opin Pediatr 2003 Feb;15(1):24-31 http://www.ncbi.nlm.nih.gov:80/entrez/query.fcgi?cmd=Retrieve&db=PubMed&list_uids=12544268&dopt=Abstract

The role of hydroxyurea in sickle cell disease.
J Haematol 2003 Jan;120(2):177-186
http://www.blackwell-synergy.com/links/doi/10.1046/j.1365-2141.2003.03849.x/full/

Related umbilical cord blood transplantation in patients with thalassemia
and sickle cell disease
Franco Locatelli, Vanderson Rocha, William Reed, Francoise Bernaudin,
Mehmet Ertem, Stelios Grafakos, Benedicte Brichard, Xiaxin Li, Arnon
Nagler, Giovanna Giorgiani, Paul R. Haut, Joel A. Brochstein, Diane J.
Nugent, Julie Blatt, Paul Woodard, Joanne Kurtzberg, Charles M. Rubin,
Roberto Miniero, Patrick Lutz, Thirumalairaj Raja, Irene Roberts,
Andrew M. Will, Isaac Yaniv, Christiane Vermylen, Nunzia Tannoia,
Federico Garnier, Irina Ionescu, Mark C. Walters, Bertram H. Lubin,
and Eliane Gluckman
Blood 2003;101 2137-2143
http://www.bloodjournal.org/cgi/content/abstract/101/6/2137?etoc

The degree of phenotypic correction of murine beta -thalassemia intermedia
following lentiviral-mediated transfer of a human gamma -globin gene is
influenced by chromosomal position effects and vector copy number
Derek A. Persons, Phillip W. Hargrove, Esther R. Allay, Hideki Hanawa,
and Arthur W. Nienhuis
Blood 2003;101 2175-2183
http://www.bloodjournal.org/cgi/content/abstract/101/6/2175?etoc

Stroke risk in siblings with sickle cell anemia
M. Catherine Driscoll, Anne Hurlet, Lori Styles, Virgil McKie,
Beatrice Files, Nancy Olivieri, Charles Pegelow, Brian Berman, Richard
Drachtman, Kantilal Patel, and Donald Brambilla
Blood 2003;101 2401-2404
http://www.bloodjournal.org/cgi/content/abstract/101/6/2401?etoc

Persistence and expression of the adenosine deaminase gene for 12 years and immune reaction to gene transfer components: long-term results of the first clinical gene therapy trial
Linda Mesler Muul, Laura M. Tuschong, Sherry Lau Soenen, G. Jayashree Jagadeesh, W. Jay Ramsey, Zhifeng Long, Charles S. Carter, Elizabeth K. Garabedian, Melinna Alleyne, Margaret Brown, Wendy Bernstein, Shepherd H. Schurman, Thomas A. Fleisher, Susan F. Leitman, Cynthia E. Dunbar, R. Michael Blaese, and Fabio Candotti
http://www.bloodjournal.org/cgi/content/abstract/101/7/2563?etoc